Bioethics News

Saving Eliza: Gene Therapy Offers New Hope for Girl with ‘Childhood Alzheimer’s’

August 17, 2016

(Today) – Eliza O’Neill’s parents call it their miracle story. After years of fundraising, 726 days of self-imposed isolation and non-stop determination to save their 6-year-old daughter’s life, she has finally become the first patient in the world to receive an experimental gene therapy for her deadly disease.

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